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Science, industry economics, patients are boosting research on rare disease drugs - and hope

...in eight months.Now the O'Neills are working with a children's hospital and a biotech firm to test a potential gene therapy, though manufacturing difficulties have delayed patient testing. The parents hope the therapy shows enough promise to...

http://chronicle.augusta.com/news/business/2015-03-25/science-industry-economics
South Carolina family achieves goal to start funding Sanfilippo syndrome trial

...degenerative disease. With greater awareness, he said, there was a chance he could gather enough funds to support a gene therapy trial at Nationwide Children's Hospital in Columbus, Ohio.O'Neill and his wife, Cara, hoped to have the $1...

http://chronicle.augusta.com/latest-news/2014-11-23/south-carolina-family-achiev
South Carolina family aims to raise $600,000 on sick daughter's birthday to help fund Sanfilippo syndrome trial

...request to make a very special birthday gift.The O'Neill family, from Columbia, has raised $1.2 million to fund a gene therapy trial for Sanfilippo syndrome, a rare and terminal degenerative disease. The family hopes to raise the remaining...

http://chronicle.augusta.com/news/metro/2014-11-14/south-carolina-family-aims-ra
Father brings efforts to save daughter Eliza to Masters

...disease. Her family, from Columbia, is on a quest to spread the video as widely as possible to raise money for a gene therapy trial at Nationwide Children's Hos pital in Columbus, Ohio. The trial, thought to be a cure for the disease, is...

http://chronicle.augusta.com/news/metro/2014-04-14/glenn-oneill-brings-efforts-s
Father brings efforts to save daughter to Masters

...disease. Her family, from Columbia, is on a quest to spread the video as widely as possible to raise funds for a gene therapy trial at Nationwide Children's Hos pital in Columbus, Ohio. The trial, thought to be a cure for the disease, is...

http://augusta.com/masters/story/news/father-brings-efforts-save-daughter-master
Blast injuries can be subtle, long-lasting

...better on a fundamental level, Dhandapani said."Then we can start targeting, going looking for those drugs or gene therapies, whatever it may be, to hopefully help these patients long-term," he said.

http://chronicle.augusta.com/news/health/2014-02-23/blast-injuries-can-be-subtle
Fish provide proof of genetic defect that leads to brain, skull malformations

...possibility of preventing or fixing the problem, he said. Likening it to an auto mechanic finding a faulty part, "then you have the possibility to replace, like a new part, (through) gene therapy or you can repair the broken part somehow."

http://chronicle.augusta.com/news/health/2012-07-05/fish-provide-proof-genetic-d
Blood vessel inhibitor identified in study

...tumor known as glioblastoma when it was delivered by gene therapy in combination with another factor that inhibits blood vessel growth, said John R. Ohlfest, the director of gene therapy at the University of Minnesota. The interest in using...

http://chronicle.augusta.com/stories/2006/10/27/met_102062.shtml
Metro
Medical College's incubator nurses biotech startups

...predisposition for cancer, for use in lab research. Revenue from the mice could be used to help finance its research concerning gene therapy for treating humans. It expects to stay in the incubator for two to three years.

http://chronicle.augusta.com/stories/2006/05/14/bus_81273.shtml
Business
Gene therapy can help ward off cancer

...precancerous cells in her cervix. A new experimental gene therapy being studied at the Medical College of Georgia...823-3213 or tom.corwin@augustachronicle.com. Gene Therapy Trial The gene therapy trial at the Medical College of Georgia is looking...

http://chronicle.augusta.com/stories/2005/12/25/met_35630.shtml
Metro